Head-to-head trial of pegunigalsidase alfa versus agalsidase beta in patients with Fabry disease and deteriorating renal function: results from the 2-year randomised phase III BALANCE study.
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J Med Genet. 2024 May 21;61(6):520-530. doi: 10.1136/jmg-2023-109445.
J Med Genet. 2024.
PMID: 37940383
Free PMC article.
Clinical Trial.