Genetic and cellular defects contributing to benign tumor formation in neurofibromatosis type 1

Hum Mol Genet. 2000 Apr 12;9(7):1059-66. doi: 10.1093/hmg/9.7.1059.

Abstract

Neurofibromatosis type 1 (NF1) is a common inherited cancer predisposition syndrome. The NF1 gene product, neurofibromin, is hypothesized to function as a tumor suppressor and nearly all NF1 patients develop benign peripheral nerve tumors. These neurofibromas presumably arise from NF1 inactivation in S100(+)Schwann cells, but there is no formal proof for this mechanism. We demonstrate that fibro-blasts isolated from neurofibromas carried at least one normal NF1 allele and expressed both NF1 mRNA and protein, whereas the S100(+)cells typically lacked the NF1 transcript. Our findings further indicate that additional molecular events aside from NF1 inactivation in Schwann cells and/or other neural crest derivatives contribute to neurofibroma formation.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adult
  • Alleles
  • Blotting, Northern
  • Blotting, Western
  • Child, Preschool
  • Female
  • Fibroblasts / metabolism
  • Genes, Neurofibromatosis 1 / genetics*
  • Humans
  • In Situ Hybridization, Fluorescence
  • Male
  • Middle Aged
  • Mutation
  • Neural Crest / metabolism
  • Neurofibroma / genetics*
  • Neurofibromatosis 1 / genetics*
  • Neurofibromatosis 1 / metabolism
  • Neurofibromin 1
  • Phenotype
  • Proteins / metabolism
  • S100 Proteins / metabolism
  • Schwann Cells / metabolism
  • Tubulin / metabolism
  • X Chromosome / genetics

Substances

  • Neurofibromin 1
  • Proteins
  • S100 Proteins
  • Tubulin