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894 results

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Page 1
Vectorized Human Antibody-Mediated Anti-Eosinophil Gene Therapy.
Gioulvanidou M, Sarklioglu S, Chen X, Lebedeva IV, Inalman Y, Pohl MA, Bourne L, Andrew D, Lorenz IC, Stiles KM, Pagovich OE, Hackett NR, Kaminsky SM, de Mulder Rougvie M, Crystal RG. Gioulvanidou M, et al. Among authors: crystal rg. Hum Gene Ther. 2024 Dec 26. doi: 10.1089/hum.2024.165. Online ahead of print. Hum Gene Ther. 2024. PMID: 39725494
Angiogenic Gene Therapy for Refractory Angina: Results of the EXACT Phase 2 Trial.
Nakamura K, Henry TD, Traverse JH, Latter DA, Mokadam NA, Answini GA, Williams AR, Sun BC, Burke CR, Bakaeen FG, DiCarli MF, Chaitman BR, Peterson MW, Byrnes DG, Ohman EM, Pepine CJ, Crystal RG, Rosengart TK, Kowalewski E, Koch GG, Dittrich HC, Povsic TJ; EXACT Trial Investigators. Nakamura K, et al. Among authors: crystal rg. Circ Cardiovasc Interv. 2024 May;17(5):e014054. doi: 10.1161/CIRCINTERVENTIONS.124.014054. Epub 2024 May 2. Circ Cardiovasc Interv. 2024. PMID: 38696284 Free PMC article. Clinical Trial.
Management of Select Adverse Events Following Delandistrogene Moxeparvovec Gene Therapy for Patients With Duchenne Muscular Dystrophy.
Zaidman CM, Goedeker NL, Aqul AA, Butterfield RJ, Connolly AM, Crystal RG, Godwin KE, Hor KN, Mathews KD, Proud CM, Kula Smyth E, Veerapandiyan A, Watkins PB, Mendell JR. Zaidman CM, et al. Among authors: crystal rg. J Neuromuscul Dis. 2024;11(3):687-699. doi: 10.3233/JND-230185. J Neuromuscul Dis. 2024. PMID: 38607761 Free PMC article.
Expression and processing of mature human frataxin after gene therapy in mice.
Rojsajjakul T, Selvan N, De B, Rosenberg JB, Kaminsky SM, Sondhi D, Janki P, Crystal RG, Mesaros C, Khanna R, Blair IA. Rojsajjakul T, et al. Among authors: crystal rg. Sci Rep. 2024 Apr 10;14(1):8391. doi: 10.1038/s41598-024-59060-0. Sci Rep. 2024. PMID: 38600238 Free PMC article.
Vessel and Airway Characteristics in One-Year Computed Tomography-defined Rapid Emphysema Progression: SPIROMICS.
Gerard SE, Dougherty TM, Nagpal P, Jin D, Han MK, Newell JD Jr, Saha PK, Comellas AP, Cooper CB, Couper D, Fortis S, Guo J, Hansel NN, Kanner RE, Kazeroni EA, Martinez FJ, Motahari A, Paine R 3rd, Rennard S, Schroeder JD, Woodruff PG, Barr RG, Smith BM, Hoffman EA; SPIROMICS Research Group. Gerard SE, et al. Ann Am Thorac Soc. 2024 Jul;21(7):1022-1033. doi: 10.1513/AnnalsATS.202304-383OC. Ann Am Thorac Soc. 2024. PMID: 38530051
Loss of Airway Phylogenetic Diversity Is Associated with Clinical and Pathobiological Markers of Disease Development in Chronic Obstructive Pulmonary Disease.
Opron K, Begley LA, Erb-Downward JR, Li G, Alexis NE, Barjaktarevic I, Barr RG, Bleecker ER, Boucher R, Bowler RP, Christenson SA, Comellas AP, Criner G, Cooper CB, Couper D, Galban CJ, Han MK, Hastie A, Hatt C, Hoffman EA, Kaner RJ, Kesimer M, Krishnan JA, LaFon DC, Martinez FJ, Ortega VE, Peters SP, Paine R 3rd, Putcha N, Woodruff PG, Huffnagle GB, Kozik AJ, Curtis JL, Huang YJ; SPIROMICS Investigators. Opron K, et al. Am J Respir Crit Care Med. 2024 Jul 15;210(2):186-200. doi: 10.1164/rccm.202303-0489OC. Am J Respir Crit Care Med. 2024. PMID: 38261629
Expression and processing of mature human frataxin after gene therapy in mice.
Rojsajjakul T, Selvan N, De B, Rosenberg JB, Kaminsky SM, Sondhi D, Janki P, Crystal RG, Mesaros C, Khanna R, Blair IA. Rojsajjakul T, et al. Among authors: crystal rg. Res Sq [Preprint]. 2023 Dec 28:rs.3.rs-3788652. doi: 10.21203/rs.3.rs-3788652/v1. Res Sq. 2023. Update in: Sci Rep. 2024 Apr 10;14(1):8391. doi: 10.1038/s41598-024-59060-0 PMID: 38234818 Free PMC article. Updated. Preprint.
Predicted deleterious variants in the human genome relevant to gene therapy with adeno-associated virus vectors.
Rostami MR, Leopold PL, Vasquez JM, de Mulder Rougvie M, Al Shakaki A, Hssain AA, Robay A, Hackett NR, Mezey JG, Crystal RG. Rostami MR, et al. Among authors: crystal rg. Mol Ther Methods Clin Dev. 2023 Oct 13;31:101136. doi: 10.1016/j.omtm.2023.101136. eCollection 2023 Dec 14. Mol Ther Methods Clin Dev. 2023. PMID: 38089635 Free PMC article.
894 results