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12 results

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Page 1
Review of clinical trials and guidelines for children and youth with mucopolysaccharidosis: outcome selection and measurement.
Howie AH, Tingley K, Inbar-Feigenberg M, Mitchell JJ, Angel K, Gentle J, Smith M, Offringa M, Butcher NJ, Campeau PM, Chakraborty P, Chan A, Fergusson D, Mamak E, McClelland P, Mercimek-Andrews S, Mhanni A, Moazin Z, Rockman-Greenberg C, Rupar CA, Skidmore B, Stockler S, Thavorn K, Wyatt A, Potter BK; INFORM RARE Network. Howie AH, et al. Orphanet J Rare Dis. 2024 Oct 23;19(1):393. doi: 10.1186/s13023-024-03364-x. Orphanet J Rare Dis. 2024. PMID: 39443985 Free PMC article. Review.
Establishing a core outcome set for mucopolysaccharidoses (MPS) in children: study protocol for a rapid literature review, candidate outcomes survey, and Delphi surveys.
Howie AH, Tingley K, Inbar-Feigenberg M, Mitchell JJ, Butcher NJ, Offringa M, Smith M, Angel K, Gentle J, Wyatt A, Campeau PM, Chan A, Chakraborty P, El Turk F, Mamak E, Mhanni A, Skidmore B, Sparkes R, Stockler S, Potter BK; INFORM RARE Network. Howie AH, et al. Trials. 2021 Nov 17;22(1):816. doi: 10.1186/s13063-021-05791-8. Trials. 2021. PMID: 34789302 Free PMC article.
Correction to: Establishing a core outcome set for mucopolysaccharidoses (MPS) in children: study protocol for a rapid literature review, candidate outcomes survey, and Delphi surveys.
Howie AH, Tingley K, Inbar-Feigenberg M, Mitchell JJ, Butcher NJ, Offringa M, Smith M, Angel K, Gentle J, Wyatt A, Campeau PM, Chan A, Chakraborty P, El Turk F, Mamak E, Mhanni A, Skidmore B, Sparkes R, Stockler S, Potter BK; INFORM RARE Network. Howie AH, et al. Trials. 2021 Dec 9;22(1):893. doi: 10.1186/s13063-021-05893-3. Trials. 2021. PMID: 34886877 Free PMC article. No abstract available.
Paper I: Heterogeneous use of registry data for participant identification and primary outcome ascertainment is found in registry-based randomized controlled trials: A scoping review.
Baba A, Tay J, Sammy A, Douglas WA, Goren K, Krause KR, Howie AH, Little J, Oskoui M, Taljaard M, Thombs BD, Potter BK, Butcher NJ, Offringa M. Baba A, et al. Among authors: howie ah. J Clin Epidemiol. 2023 Jul;159:289-299. doi: 10.1016/j.jclinepi.2023.04.016. Epub 2023 May 3. J Clin Epidemiol. 2023. PMID: 37146658 Review.
Paper II: thematic framework analysis of registry-based randomized controlled trials provided insights for designing trial ready registries.
Krause KR, Tay J, Douglas WA, Sammy A, Baba A, Goren K, Thombs BD, Howie AH, Oskoui M, Frøbert O, Trakadis Y, Little J, Potter BK, Butcher NJ, Offringa M. Krause KR, et al. Among authors: howie ah. J Clin Epidemiol. 2023 Jul;159:330-343. doi: 10.1016/j.jclinepi.2023.04.015. Epub 2023 May 4. J Clin Epidemiol. 2023. PMID: 37146660 Review.
Addressing the disconnect between trial intention and design.
Howie A, Taljaard M, Moon PM, Nightingale N, Zwarenstein M. Howie A, et al. Lancet Glob Health. 2021 May;9(5):e577-e578. doi: 10.1016/S2214-109X(20)30543-X. Epub 2021 Jan 15. Lancet Glob Health. 2021. PMID: 33460560 Free article. Review. No abstract available.
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