Accelerated Endosomal Escape of Splice-Switching Oligonucleotides Enables Efficient Hepatic Splice Correction.
Weiss S, Decker S, Kugler C, Gómez LB, Fasching H, Benisch D, Alioglu F, Ferencz L, Birkfeld T, Ilievski F, Baumann V, Duran A, Dusinovic E, Follrich N, Milenkovic S, Mihalicokova D, Paunov D, Singeorzan K, Zehetmayer N, Zivanonvic D, Lächelt U, Boersma A, Rülicke T, Sami H, Ogris M.
Weiss S, et al. Among authors: decker s.
ACS Appl Mater Interfaces. 2025 Jan 28. doi: 10.1021/acsami.4c19340. Online ahead of print.
ACS Appl Mater Interfaces. 2025.
PMID: 39873730