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Evaluation of a rapid multi-attribute combinatorial high-throughput UV-Vis/DLS/SLS analytical platform for rAAV quantification and characterization.
Liu X, Jean-Gilles R, Baginski J, Cai C, Yan R, Zhang L, Lance K, van der Loo JCM, Davidson BL. Liu X, et al. Among authors: van der loo jcm. Mol Ther Methods Clin Dev. 2024 Jul 15;32(3):101298. doi: 10.1016/j.omtm.2024.101298. eCollection 2024 Sep 12. Mol Ther Methods Clin Dev. 2024. PMID: 39170800 Free PMC article.
Preclinical Evaluation of Foamy Virus Vector-Mediated Gene Addition in Human Hematopoietic Stem/Progenitor Cells for Correction of Leukocyte Adhesion Deficiency Type 1.
Smith RH, Bloomer H, Fink D, Keyvanfar K, Nasimuzzaman M, Sancheznieto F, Dutta R, Guenther Bui K, Alvarado LJ, Bauer TR Jr, Hickstein DD, Russell DW, Malik P, van der Loo JCM, Highfill SL, Kuhns DB, Pirooznia M, Larochelle A. Smith RH, et al. Among authors: van der loo jcm. Hum Gene Ther. 2022 Dec;33(23-24):1293-1304. doi: 10.1089/hum.2022.065. Epub 2022 Nov 1. Hum Gene Ther. 2022. PMID: 36094106 Free PMC article.
Selecting a Cell Engineering Methodology During Cell Therapy Product Development.
Timmins LM, Burr AM, Carroll K, Keefe R, Teryek M, Cantolupo LJ, van der Loo JCM, Heathman TRJ, Gormley A, Smith D, Parekkadan B. Timmins LM, et al. Among authors: van der loo jcm. Cell Transplant. 2021 Jan-Dec;30:9636897211003022. doi: 10.1177/09636897211003022. Cell Transplant. 2021. PMID: 34013781 Free PMC article. Review.
The clinical landscape for AAV gene therapies.
Kuzmin DA, Shutova MV, Johnston NR, Smith OP, Fedorin VV, Kukushkin YS, van der Loo JCM, Johnstone EC. Kuzmin DA, et al. Among authors: van der loo jcm. Nat Rev Drug Discov. 2021 Mar;20(3):173-174. doi: 10.1038/d41573-021-00017-7. Nat Rev Drug Discov. 2021. PMID: 33495615 No abstract available.
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
George LA, Sullivan SK, Giermasz A, Rasko JEJ, Samelson-Jones BJ, Ducore J, Cuker A, Sullivan LM, Majumdar S, Teitel J, McGuinn CE, Ragni MV, Luk AY, Hui D, Wright JF, Chen Y, Liu Y, Wachtel K, Winters A, Tiefenbacher S, Arruda VR, van der Loo JCM, Zelenaia O, Takefman D, Carr ME, Couto LB, Anguela XM, High KA. George LA, et al. Among authors: van der loo jcm. N Engl J Med. 2017 Dec 7;377(23):2215-2227. doi: 10.1056/NEJMoa1708538. N Engl J Med. 2017. PMID: 29211678 Free PMC article. Clinical Trial.
The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute.
Flotte TR, Daniels E, Benson J, Bevett-Rose JM, Cornetta K, Diggins M, Johnston J, Sepelak S, van der Loo JCM, Wilson JM, McDonald CL. Flotte TR, et al. Among authors: van der loo jcm. Hum Gene Ther Clin Dev. 2017 Dec;28(4):178-186. doi: 10.1089/humc.2017.170. Epub 2017 Nov 27. Hum Gene Ther Clin Dev. 2017. PMID: 29130351 Free PMC article.
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