SRSF1-dependent nuclear export inhibition of C9ORF72 repeat transcripts prevents neurodegeneration and associated motor deficits.
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Hautbergue GM, et al. Among authors: dodd je.
Nat Commun. 2017 Jul 5;8:16063. doi: 10.1038/ncomms16063.
Nat Commun. 2017.
PMID: 28677678
Free PMC article.