CPEB alteration and aberrant transcriptome-polyadenylation lead to a treatable SLC19A3 deficiency in Huntington's disease.
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Picó S, et al. Among authors: lucas jj.
Sci Transl Med. 2021 Sep 29;13(613):eabe7104. doi: 10.1126/scitranslmed.abe7104. Epub 2021 Sep 29.
Sci Transl Med. 2021.
PMID: 34586830
Free article.