ABE8e adenine base editor precisely and efficiently corrects a recurrent COL7A1 nonsense mutation.
Sheriff A, Guri I, Zebrowska P, Llopis-Hernandez V, Brooks IR, Tekkela S, Subramaniam K, Gebrezgabher R, Naso G, Petrova A, Balon K, Onoufriadis A, Kujawa D, Kotulska M, Newby G, Łaczmański Ł, Liu DR, McGrath JA, Jacków J.
Sheriff A, et al. Among authors: kujawa d.
Sci Rep. 2022 Nov 16;12(1):19643. doi: 10.1038/s41598-022-24184-8.
Sci Rep. 2022.
PMID: 36385635
Free PMC article.