SPLICER: A Highly Efficient Base Editing Toolbox That Enables In Vivo Therapeutic Exon Skipping.
Miskalis A, Shirguppe S, Winter J, Elias G, Swami D, Nambiar A, Stilger M, Woods WS, Gosstola N, Gapinske M, Zeballos A, Moore H, Maslov S, Gaj T, Perez-Pinera P.
Miskalis A, et al.
bioRxiv [Preprint]. 2024 Apr 2:2024.04.01.587650. doi: 10.1101/2024.04.01.587650.
bioRxiv. 2024.
PMID: 38883727
Free PMC article.
Updated.
Preprint.