Adeno-associated virus-based gene therapy for hemophilia-addressing the gaps.
Miesbach W, Batty P, Chowdary P, Fong S, Kaczmarek R, Leebeek FWG, Long B, Mahlangu J, Makris M, Pierce GF, Pipe SW, Srivastava A, Voorberg J, Peyvandi F.
Miesbach W, et al. Among authors: long b.
Res Pract Thromb Haemost. 2024 Dec 31;9(1):102673. doi: 10.1016/j.rpth.2024.102673. eCollection 2025 Jan.
Res Pract Thromb Haemost. 2024.
PMID: 39895992
Free PMC article.
Review.