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Assessing age of onset and clinical symptoms over time in patients with heterozygous pathogenic DHDDS variants.
J Inherit Metab Dis. 2024 Sep;47(5):935-944. doi: 10.1002/jimd.12769. Epub 2024 Jun 21.
J Inherit Metab Dis. 2024.
PMID: 39540616
Review.
Liposome-encapsulated mannose-1-phosphate therapy improves global N-glycosylation in different congenital disorders of glycosylation.
Budhraja R, Radenkovic S, Jain A, Muffels IJJ, Ismaili MHA, Kozicz T, Pandey A, Morava E.
Budhraja R, et al. Among authors: muffels ijj.
Mol Genet Metab. 2024 Jun;142(2):108487. doi: 10.1016/j.ymgme.2024.108487. Epub 2024 May 7.
Mol Genet Metab. 2024.
PMID: 38733638
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Bi-allelic variants in NAE1 cause intellectual disability, ischiopubic hypoplasia, stress-mediated lymphopenia and neurodegeneration.
Muffels IJJ, Schene IF, Rehmann H, Massink MPG, van der Wal MM, Bauder C, Labeur M, Armando NG, Lequin MH, Houben ML, Giltay JC, Haitjema S, Huisman A, Vansenne F, Bluvstein J, Pappas J, Shailee LV, Zarate YA, Mokry M, van Haaften GW, Nieuwenhuis EES, Refojo D, van Wijk F, Fuchs SA, van Hasselt PM.
Muffels IJJ, et al.
Am J Hum Genet. 2023 Jan 5;110(1):146-160. doi: 10.1016/j.ajhg.2022.12.003.
Am J Hum Genet. 2023.
PMID: 36608681
Free PMC article.
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NAA80 bi-allelic missense variants result in high-frequency hearing loss, muscle weakness and developmental delay.
Muffels IJJ, Wiame E, Fuchs SA, Massink MPG, Rehmann H, Musch JLI, Van Haaften G, Vertommen D, van Schaftingen E, van Hasselt PM.
Muffels IJJ, et al.
Brain Commun. 2021 Oct 26;3(4):fcab256. doi: 10.1093/braincomms/fcab256. eCollection 2021.
Brain Commun. 2021.
PMID: 34805998
Free PMC article.
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