Low-dose AAV-CRISPR-mediated liver-specific knock-in restored hemostasis in neonatal hemophilia B mice with subtle antibody response.
He X, Zhang Z, Xue J, Wang Y, Zhang S, Wei J, Zhang C, Wang J, Urip BA, Ngan CC, Sun J, Li Y, Lu Z, Zhao H, Pei D, Li CK, Feng B.
He X, et al. Among authors: ngan cc.
Nat Commun. 2022 Nov 25;13(1):7275. doi: 10.1038/s41467-022-34898-y.
Nat Commun. 2022.
PMID: 36434000
Free PMC article.