BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression.
Konkle BA, Walsh CE, Escobar MA, Josephson NC, Young G, von Drygalski A, McPhee SWJ, Samulski RJ, Bilic I, de la Rosa M, Reipert BM, Rottensteiner H, Scheiflinger F, Chapin JC, Ewenstein B, Monahan PE.
Konkle BA, et al. Among authors: reipert bm.
Blood. 2021 Feb 11;137(6):763-774. doi: 10.1182/blood.2019004625.
Blood. 2021.
PMID: 33067633
Free PMC article.
Clinical Trial.