JEWELFISH: 24-month results from an open-label study in non-treatment-naïve patients with SMA receiving treatment with risdiplam.
Chiriboga CA, Bruno C, Duong T, Fischer D, Mercuri E, Kirschner J, Kostera-Pruszczyk A, Jaber B, Gorni K, Kletzl H, Carruthers I, Martin C, Scalco RS, Fontoura P, Muntoni F; JEWELFISH Study Group.
Chiriboga CA, et al. Among authors: scalco rs.
J Neurol. 2024 Aug;271(8):4871-4884. doi: 10.1007/s00415-024-12318-z. Epub 2024 May 11.
J Neurol. 2024.
PMID: 38733387
Free PMC article.