Clinical effect and safety profile of pegzilarginase in patients with arginase 1 deficiency.
Diaz GA, Schulze A, McNutt MC, Leão-Teles E, Merritt JL 2nd, Enns GM, Batzios S, Bannick A, Zori RT, Sloan LS, Potts SL, Bubb G, Quinn AG.
Diaz GA, et al. Among authors: bubb g.
J Inherit Metab Dis. 2021 Jul;44(4):847-856. doi: 10.1002/jimd.12343. Epub 2021 Jan 26.
J Inherit Metab Dis. 2021.
PMID: 33325055
Free PMC article.
Clinical Trial.