Pacak CA - Search Results

1

Blunted fat oxidation upon submaximal exercise is partially compensated by enhanced glucose metabolism in children, adolescents, and young adults with Barth syndrome.

Cade WT, Bohnert KL, Peterson LR, Patterson BW, Bittel AJ, Okunade AL, de las Fuentes L, Steger-May K, Bashir A, Schweitzer GG, Chacko SK, Wanders RJ, Pacak CA, Byrne BJ, Reeds DN. Cade WT, et al. Among authors: pacak ca. J Inherit Metab Dis. 2019 May;42(3):480-493. doi: 10.1002/jimd.12094. Epub 2019 Apr 11. J Inherit Metab Dis. 2019. PMID: 30924938 Free PMC article.

2

Sustained correction of glycogen storage disease type II using adeno-associated virus serotype 1 vectors.

Mah C, Cresawn KO, Fraites TJ Jr, Pacak CA, Lewis MA, Zolotukhin I, Byrne BJ. Mah C, et al. Among authors: pacak ca. Gene Ther. 2005 Sep;12(18):1405-9. doi: 10.1038/sj.gt.3302550. Gene Ther. 2005. PMID: 15920463

3

Physiological correction of Pompe disease by systemic delivery of adeno-associated virus serotype 1 vectors.

Mah C, Pacak CA, Cresawn KO, Deruisseau LR, Germain S, Lewis MA, Cloutier DA, Fuller DD, Byrne BJ. Mah C, et al. Among authors: pacak ca. Mol Ther. 2007 Mar;15(3):501-7. doi: 10.1038/sj.mt.6300100. Epub 2007 Jan 23. Mol Ther. 2007. PMID: 17245350 Free article.

4

Long-term skeletal muscle protection after gene transfer in a mouse model of LGMD-2D.

Pacak CA, Walter GA, Gaidosh G, Bryant N, Lewis MA, Germain S, Mah CS, Campbell KP, Byrne BJ. Pacak CA, et al. Mol Ther. 2007 Oct;15(10):1775-81. doi: 10.1038/sj.mt.6300246. Epub 2007 Jul 24. Mol Ther. 2007. PMID: 17653106 Free article.

5

Tissue specific promoters improve specificity of AAV9 mediated transgene expression following intra-vascular gene delivery in neonatal mice.

Pacak CA, Sakai Y, Thattaliyath BD, Mah CS, Byrne BJ. Pacak CA, et al. Genet Vaccines Ther. 2008 Sep 23;6:13. doi: 10.1186/1479-0556-6-13. Genet Vaccines Ther. 2008. PMID: 18811960 Free PMC article.

6

Relative persistence of AAV serotype 1 vector genomes in dystrophic muscle.

Pacak CA, Conlon T, Mah CS, Byrne BJ. Pacak CA, et al. Genet Vaccines Ther. 2008 Oct 15;6:14. doi: 10.1186/1479-0556-6-14. Genet Vaccines Ther. 2008. PMID: 18854054 Free PMC article.

7

AAV vectors for cardiac gene transfer: experimental tools and clinical opportunities.

Pacak CA, Byrne BJ. Pacak CA, et al. Mol Ther. 2011 Sep;19(9):1582-90. doi: 10.1038/mt.2011.124. Epub 2011 Jul 26. Mol Ther. 2011. PMID: 21792180 Free PMC article. Review.

8

Transfer of Therapeutic Genes into Fetal Rhesus Monkeys Using Recombinant Adeno-Associated Type I Viral Vectors.

Conlon TJ, Mah CS, Pacak CA, Rucker Henninger MB, Erger KE, Jorgensen ML, Lee CC, Tarantal AF, Byrne BJ. Conlon TJ, et al. Among authors: pacak ca. Hum Gene Ther Clin Dev. 2016 Dec;27(4):152-159. doi: 10.1089/humc.2016.119. Hum Gene Ther Clin Dev. 2016. PMID: 27855487 Free PMC article.

9

Impaired cardiac and skeletal muscle bioenergetics in children, adolescents, and young adults with Barth syndrome.

Bashir A, Bohnert KL, Reeds DN, Peterson LR, Bittel AJ, de las Fuentes L, Pacak CA, Byrne BJ, Cade WT. Bashir A, et al. Among authors: pacak ca. Physiol Rep. 2017 Feb;5(3):e13130. doi: 10.14814/phy2.13130. Physiol Rep. 2017. PMID: 28196853 Free PMC article.

10

AAV-Mediated TAZ Gene Replacement Restores Mitochondrial and Cardioskeletal Function in Barth Syndrome.

Suzuki-Hatano S, Saha M, Rizzo SA, Witko RL, Gosiker BJ, Ramanathan M, Soustek MS, Jones MD, Kang PB, Byrne BJ, Cade WT, Pacak CA. Suzuki-Hatano S, et al. Among authors: pacak ca. Hum Gene Ther. 2019 Feb;30(2):139-154. doi: 10.1089/hum.2018.020. Epub 2018 Oct 3. Hum Gene Ther. 2019. PMID: 30070157 Free PMC article.

Save citations to file

Email citations

Send citations to clipboard

Add to Collections

Add to My Bibliography

Create a file for external citation management software

Your saved search

Your RSS Feed

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Article Language

Species

Sex

Age

Other

67 results

Search Page

Filters