Gel-mediated delivery of AAV1 vectors corrects ventilatory function in Pompe mice with established disease.
Mah CS, Falk DJ, Germain SA, Kelley JS, Lewis MA, Cloutier DA, DeRuisseau LR, Conlon TJ, Cresawn KO, Fraites TJ Jr, Campbell-Thompson M, Fuller DD, Byrne BJ.
Mah CS, et al. Among authors: kelley js.
Mol Ther. 2010 Mar;18(3):502-10. doi: 10.1038/mt.2009.305. Epub 2010 Jan 26.
Mol Ther. 2010.
PMID: 20104213
Free PMC article.