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Multiple Integrated Non-clinical Studies Predict the Safety of Lentivirus-Mediated Gene Therapy for β-Thalassemia.
Lidonnici MR, Paleari Y, Tiboni F, Mandelli G, Rossi C, Vezzoli M, Aprile A, Lederer CW, Ambrosi A, Chanut F, Sanvito F, Calabria A, Poletti V, Mavilio F, Montini E, Naldini L, Cristofori P, Ferrari G. Lidonnici MR, et al. Among authors: lederer cw. Mol Ther Methods Clin Dev. 2018 Sep 13;11:9-28. doi: 10.1016/j.omtm.2018.09.001. eCollection 2018 Dec 14. Mol Ther Methods Clin Dev. 2018. PMID: 30320151 Free PMC article.
Bone marrow as an alternative site for islet transplantation.
Cantarelli E, Melzi R, Mercalli A, Sordi V, Ferrari G, Lederer CW, Mrak E, Rubinacci A, Ponzoni M, Sitia G, Guidotti LG, Bonifacio E, Piemonti L. Cantarelli E, et al. Among authors: lederer cw. Blood. 2009 Nov 12;114(20):4566-74. doi: 10.1182/blood-2009-03-209973. Epub 2009 Sep 22. Blood. 2009. PMID: 19773545 Free article.
Recent trends in the gene therapy of β-thalassemia.
Finotti A, Breda L, Lederer CW, Bianchi N, Zuccato C, Kleanthous M, Rivella S, Gambari R. Finotti A, et al. Among authors: lederer cw. J Blood Med. 2015 Feb 19;6:69-85. doi: 10.2147/JBM.S46256. eCollection 2015. J Blood Med. 2015. PMID: 25737641 Free PMC article. Review.
Selection and Identification of Skeletal-Muscle-Targeted RNA Aptamers.
Philippou S, Mastroyiannopoulos NP, Makrides N, Lederer CW, Kleanthous M, Phylactou LA. Philippou S, et al. Among authors: lederer cw. Mol Ther Nucleic Acids. 2018 Mar 2;10:199-214. doi: 10.1016/j.omtn.2017.12.004. Epub 2017 Dec 9. Mol Ther Nucleic Acids. 2018. PMID: 29499933 Free PMC article.
56 results