Gene therapy for glycogen storage diseases.
Koeberl DD, Koch RL, Lim JA, Brooks ED, Arnson BD, Sun B, Kishnani PS.
Koeberl DD, et al. Among authors: arnson bd.
J Inherit Metab Dis. 2024 Jan;47(1):93-118. doi: 10.1002/jimd.12654. Epub 2023 Jul 27.
J Inherit Metab Dis. 2024.
PMID: 37421310
Free PMC article.
Review.