Sustained knockdown of a disease-causing gene in patient-specific induced pluripotent stem cells using lentiviral vector-based gene therapy.
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Eggenschwiler R, et al. Among authors: cantz t.
Stem Cells Transl Med. 2013 Sep;2(9):641-54. doi: 10.5966/sctm.2013-0017. Epub 2013 Aug 7.
Stem Cells Transl Med. 2013.
PMID: 23926210
Free PMC article.