Gene therapy in transfusion-dependent non-β0/β0 genotype β-thalassemia: first real-world experience of beti-cel.
Mirza A, Ritsert ML, Tao G, Thakar H, Lobitz S, Heine S, Koscher L, Dürken M, Schmitt A, Schmitt M, Pavel P, Laier S, Jakoby D, Greil J, Kunz J, Kulozik A.
Mirza A, et al. Among authors: heine s.
Blood Adv. 2025 Jan 14;9(1):29-38. doi: 10.1182/bloodadvances.2024014104.
Blood Adv. 2025.
PMID: 39418614