Antisense inhibition of AT1 receptor in vascular smooth muscle cells using adeno-associated virus-based vector

Hypertension. 1999 Jan;33(1 Pt 2):354-9. doi: 10.1161/01.hyp.33.1.354.

Abstract

Vascular smooth muscle cells (VSMCs) are the main peripheral target for vasoconstriction and growth-promoting activity of angiotensin II (Ang II), acting through angiotensin type 1 receptors (AT1-R). Current antihypertension treatments include daily reductions in the effects of Ang II. To decrease an effect of Ang II in a prolonged fashion, we have developed an adeno-associated virus (AAV) vector with antisense DNA for AT1-R. AAV has many advantages over other viral vectors. AAV is nonpathogenic, does not stimulate inflammation or immune reaction and enters nondividing cells, and provides stable long-term gene expression. To test AAV in VSMCs, we constructed and tested plasmid AAV (pAAV) and recombinant AAV (rAAV) with AT1-R antisense DNA. rAAV was constructed with a cassette containing a cytomegalovirus promoter and the cDNA for the AT1-R inserted in the antisense direction. The cassette was packaged into the virion. Transfection of VSMCs with the pAAV antisense to AT1-R produced a significant reduction in the amount of AT1-R (P<0.01). Transduction of VSMCs with the rAAV-AT1-R-AS at MOI of 5 also showed significant reduction of AT1-R and long-lasting expression of the transgene for at least 8 weeks. The reduction of AT1-R number in VSMCs was concomitant with a decrease in the Ang II-stimulated increase of intracellular calcium. The results show that AAV vector delivers AT1-R antisense to inhibit AT1-R in VSMCs. For the purpose of gene therapy for hypertension, it is necessary to demonstrate the effectiveness of a vector system in VSMCs. This study provides support for the potential use of AAV AT1-R antisense in VSMCs.

Publication types

  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Angiotensin II / pharmacology
  • Angiotensin Receptor Antagonists
  • Animals
  • Aorta, Thoracic / cytology
  • Aorta, Thoracic / drug effects
  • Aorta, Thoracic / physiology*
  • Calcium / metabolism
  • Cell Line
  • Cells, Cultured
  • Cytomegalovirus / genetics
  • DNA, Antisense / genetics
  • DNA, Antisense / pharmacology*
  • DNA, Complementary
  • Dependovirus
  • Genes, Reporter
  • Genetic Vectors
  • Green Fluorescent Proteins
  • Humans
  • Luminescent Proteins / genetics
  • Muscle, Smooth, Vascular / cytology
  • Muscle, Smooth, Vascular / drug effects
  • Muscle, Smooth, Vascular / physiology*
  • Phenylephrine / pharmacology
  • Promoter Regions, Genetic
  • Rats
  • Receptor, Angiotensin, Type 1
  • Receptor, Angiotensin, Type 2
  • Receptors, Angiotensin / genetics
  • Receptors, Angiotensin / physiology*
  • Recombinant Proteins / biosynthesis
  • Reverse Transcriptase Polymerase Chain Reaction
  • Transfection

Substances

  • Angiotensin Receptor Antagonists
  • DNA, Antisense
  • DNA, Complementary
  • Luminescent Proteins
  • Receptor, Angiotensin, Type 1
  • Receptor, Angiotensin, Type 2
  • Receptors, Angiotensin
  • Recombinant Proteins
  • Angiotensin II
  • Green Fluorescent Proteins
  • Phenylephrine
  • Calcium