Dual blockade of cyclic AMP response element- (CRE) and AP-1-directed transcription by CRE-transcription factor decoy oligonucleotide. gene-specific inhibition of tumor growth

J Biol Chem. 1999 Jan 15;274(3):1573-80. doi: 10.1074/jbc.274.3.1573.

Abstract

Alteration of gene transcription by inhibition of specific transcriptional regulatory proteins has important therapeutic potential. Synthetic double-stranded phosphorothioate oligonucleotides with high affinity for a target transcription factor can be introduced into cells as decoy cis-elements to bind the factors and alter gene expression. The CRE (cyclic AMP response element)-transcription factor complex is a pleiotropic activator that participates in the induction of a wide variety of cellular and viral genes. Because the CRE cis-element, TGACGTCA, is palindromic, a synthetic single-stranded oligonucleotide composed of the CRE sequence self-hybridizes to form a duplex/hairpin. Herein we report that the CRE-palindromic oligonucleotide can penetrate into cells, compete with CRE enhancers for binding transcription factors, and specifically interfere with CRE- and AP-1-directed transcription in vivo. These oligonucleotides restrained tumor cell proliferation, without affecting the growth of noncancerous cells. This decoy oligonucleotide approach offers great promise as a tool for defining cellular regulatory processes and treating cancer and other diseases.

MeSH terms

  • Blotting, Western
  • Cyclic AMP Response Element-Binding Protein / antagonists & inhibitors*
  • Cyclic AMP Response Element-Binding Protein / genetics*
  • DNA / metabolism
  • Enhancer Elements, Genetic
  • Gene Expression Regulation, Neoplastic / drug effects*
  • Humans
  • Nucleic Acid Conformation
  • Oligonucleotides, Antisense / pharmacology*
  • Transcription Factor AP-1 / antagonists & inhibitors*
  • Transcription, Genetic / drug effects*
  • Tumor Cells, Cultured

Substances

  • Cyclic AMP Response Element-Binding Protein
  • Oligonucleotides, Antisense
  • Transcription Factor AP-1
  • DNA