Ex vivo breast cancer cell purging by adenovirus-mediated cytosine deaminase gene transfer and short-term incubation with 5-fluorocytosine completely prevents tumor growth after transplantation

Hum Gene Ther. 1998 Oct 10;9(15):2277-84. doi: 10.1089/hum.1998.9.15-2277.

Abstract

Peripheral blood progenitor harvests of breast cancer patients are contaminated with tumor cells, suggesting a potential role for these cells in the relapse after high-dose chemotherapy. Whereas physical purging methods do not eliminate contaminating tumor cells completely, pharmacological purging, although highly efficient, is hampered by a strong nonspecific toxicity toward hematopoietic progenitor cells. Taking advantage of the high efficiency of adenovirus-mediated gene transfer to epithelial cells, we selectively loaded breast cancer cells in vitro with a cytotoxic drug by gene transfer of the prodrug-converting enzyme cytosine deaminase (AdCMV.CD) and 5-fluorocytosine (5-FC). Despite the low dose of vector administered, limited exposure to 5-FC, and transplantation only of viable tumor cells into SCID mice, all animals that received cells treated in vitro with AdCMV.CD plus 5-FC were completely free of tumor development. These data show that the selective loading of tumor cells with AdCMV.CD/5-FC might be useful for purging of autografts.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenoviridae / enzymology
  • Adenoviridae / genetics*
  • Animals
  • Antigens, CD34 / analysis
  • Breast Neoplasms / pathology*
  • Cytosine Deaminase
  • Female
  • Flucytosine / metabolism
  • Flucytosine / pharmacology*
  • Fluorouracil / pharmacology
  • Gene Transfer Techniques*
  • Genetic Vectors*
  • Hematopoietic Stem Cells / immunology
  • Humans
  • Mice
  • Mice, SCID
  • Neoplasm Transplantation
  • Nucleoside Deaminases / genetics*
  • Nucleoside Deaminases / metabolism
  • Prodrugs / metabolism
  • Prodrugs / pharmacology
  • Tumor Cells, Cultured

Substances

  • Antigens, CD34
  • Prodrugs
  • Flucytosine
  • Nucleoside Deaminases
  • Cytosine Deaminase
  • Fluorouracil