Favorable long-term cognitive outcomes following recurrent ARIA linked to amyloid-lowering therapies: two cases

J Neurol. 2025 Jan 24;272(2):168. doi: 10.1007/s00415-025-12910-x.

Abstract

Introduction: The large-scale approval of anti-amyloid monoclonal antibodies for treating Alzheimer's disease (AD) has raised concerns about their safety due to treatment-emergent amyloid-related imaging abnormalities (ARIA).

Methods: We present two cases of patients diagnosed with mild cognitive impairment due to AD who were enrolled in the GRADUATE I clinical trial. They received subcutaneous gantenerumab every two weeks during the study period.

Results: Both patients experienced recurrent ARIA-Effusion/Edema type (ARIA-E). One developed symptomatic and severe ARIA, leading to hospitalization and study withdrawal. We report a long follow-up post-randomization (65 and 54 months), during which the adverse events did not appear to have a negative impact on disease progression. Additionally, one patient had a negative amyloid-PET over a year after treatment cessation.

Discussion: These cases suggest that recurrent ARIA-E do not inevitably lead to accelerated progression, instead, may relate to possible long-term benefits. The mechanisms underlying these findings warrant further real-life evidence.

Keywords: Alzheimer’s disease (AD); Amyloid-related imaging abnormalities (ARIA); Anti-amyloid monoclonal antibodies; Gantenerumab.

Publication types

  • Case Reports

MeSH terms

  • Aged
  • Aged, 80 and over
  • Alzheimer Disease* / drug therapy
  • Antibodies, Monoclonal, Humanized* / administration & dosage
  • Antibodies, Monoclonal, Humanized* / adverse effects
  • Cognitive Dysfunction* / drug therapy
  • Cognitive Dysfunction* / etiology
  • Disease Progression
  • Female
  • Follow-Up Studies
  • Humans
  • Male
  • Positron-Emission Tomography
  • Recurrence

Substances

  • Antibodies, Monoclonal, Humanized
  • gantenerumab