Masking in Active Comparator Designs in Pharmacovigilance: A Retrospective Bias Analysis on the Spontaneous Reporting of Thiazolidinediones and Cardiovascular Events

Pharmacoepidemiol Drug Saf. 2025 Jan;34(1):e70102. doi: 10.1002/pds.70102.

Abstract

Introduction: Masking is a reporting bias where drug safety signals are muffled by elevated reporting of other medications in spontaneous reporting databases. While the impact of masking is often limited, its effect when using restricted designs, such as active comparators, can be consequential.

Methods: We used data from the US Food and Drugs Administration Adverse Event Reporting System (1999Q3-2013Q3) to study masking in a real-world example. Rosiglitazone, a thiazolidinedione with elevated reporting after safety concerns over cardiovascular risks, was the masking candidate. We hypothesized that stimulated reporting masked signals for another thiazolidinedione, pioglitazone. We computed estimates of proportional reporting ratios and information components, using the Bayesian confidence propagation neural network, for pioglitazone-myocardial infarction and pioglitazone-cardiac failure under unrestricted and active comparator designs, with and without the mask, before (1999Q3-2007Q1) and after (2007Q2-2013Q3) safety concerns. Relative change-in-estimates were computed to compare results with and without rosiglitazone.

Results: From 1999Q3-2007Q1, relative change-in-estimates of proportional reporting ratio for pioglitazone-myocardial infarction was 0.00 in unrestricted design and 0.10 in active comparator, and for pioglitazone-cardiac failure, the change was 0.01 and 0.62, respectively. From 2007Q2-2013Q3, relative change-in-estimates for pioglitazone-myocardial infarction was 0.41 in unrestricted design and 18.00 in active comparator; the change for pioglitazone-cardiac failure was 0.04 and 1.03, respectively. Relative changes in estimates of information component mirrored these trends.

Conclusions: Masking can influence signal detection in active comparator designs where external events impact reporting rates in reference sets. Evaluating masking in related contexts is essential for drug safety monitoring and resource allocation for follow-up studies.

Keywords: bias; cardiovascular risks; data analysis; diabetes mellitus; methodology; pharmacovigilance; safety.

MeSH terms

  • Adverse Drug Reaction Reporting Systems* / statistics & numerical data
  • Bayes Theorem
  • Bias
  • Cardiovascular Diseases / chemically induced
  • Cardiovascular Diseases / epidemiology
  • Databases, Factual / statistics & numerical data
  • Heart Failure / chemically induced
  • Heart Failure / epidemiology
  • Humans
  • Hypoglycemic Agents* / adverse effects
  • Myocardial Infarction / chemically induced
  • Myocardial Infarction / epidemiology
  • Pharmacovigilance*
  • Pioglitazone* / adverse effects
  • Research Design
  • Retrospective Studies
  • Rosiglitazone* / adverse effects
  • Thiazolidinediones* / adverse effects
  • United States / epidemiology
  • United States Food and Drug Administration*

Substances

  • Thiazolidinediones
  • Pioglitazone
  • Rosiglitazone
  • Hypoglycemic Agents