Dosing Regimen Recommendations for Sirolimus in Adult Liver Transplant Recipients: Insights from a Population Pharmacokinetic Model

Drug Des Devel Ther. 2024 Dec 28:18:6379-6388. doi: 10.2147/DDDT.S503463. eCollection 2024.

Abstract

Background: Sirolimus is a commonly used immunosuppressant administered after solid organ transplantation. It is characterized by a narrow therapeutic window and highly variable exposure, necessitating the identification of the sources of variability and design of individualized drug therapies.

Aim: This study aimed to perform a population pharmacokinetic (PK) analysis of sirolimus in adult liver transplant recipients and develop dosing regimen recommendations according to patient characteristics.

Methodology: A total of 216 measurements of whole blood sirolimus concentrations in 103 adult patients were obtained for analysis. Covariates influencing the PKs of sirolimus were investigated using a stepwise procedure. Monte Carlo simulations were conducted to recommend dosing regimens for patients with different levels of covariates.

Results: A one-compartment model with first-order elimination provided the best fit of the data. Hematocrit (HCT) significantly influenced the apparent clearance of sirolimus. Monte Carlo simulations showed that for patients with a low HCT level of 28%, dosing regimens of 1.5 mg qd or 1 mg qd alternating with 1.5 mg qd should be recommended. For patients with a normal HCT level, the recommended dosing regimens were 1 mg qd, 2 mg qod, or 0.5 mg qd alternating with 1 mg qd.

Conclusion: Based on our population PK model of sirolimus in adult liver transplant recipients, which has the largest sample size to date, we recommend to tailor dosing regimens to various HCT levels in such patients.

Keywords: dosing regimen; hematocrit; liver transplant; population pharmacokinetic analysis; sirolimus.

MeSH terms

  • Adult
  • Aged
  • Dose-Response Relationship, Drug*
  • Female
  • Humans
  • Immunosuppressive Agents* / administration & dosage
  • Immunosuppressive Agents* / blood
  • Immunosuppressive Agents* / pharmacokinetics
  • Liver Transplantation*
  • Male
  • Middle Aged
  • Models, Biological
  • Monte Carlo Method*
  • Sirolimus* / administration & dosage
  • Sirolimus* / blood
  • Sirolimus* / pharmacokinetics
  • Young Adult

Substances

  • Sirolimus
  • Immunosuppressive Agents

Grants and funding

This research did not receive any specific grant from funding agencies in the public, commercial, or not-for-profit sectors.