Current status of fluid biomarkers for early Alzheimer's disease and FDA regulation implications

J Neurol Sci. 2024 Dec 15:467:123325. doi: 10.1016/j.jns.2024.123325. Epub 2024 Nov 22.

Abstract

Many changes can now be seen in the development and use of tests, especially those incorporating fluid biomarkers, to diagnose Alzheimer's disease (AD), a devastating disease caused by the progressive but rapid degeneration of cortical tissue. Some biomarkers we already know have a significant association with AD, such as amyloid beta (Aβ) and tau, as well as the ratio of concentrations of other Aβ isoforms. In addition, several novel biomarkers are emerging that can also be used as diagnostic fluid biomarkers for AD, but many studies are still needed before we can consider them reliable. The U.S. Federal Food and Drug Administration recently announced its final ruling to regulate laboratory-developed tests (LDTs) as medical devices, which can significantly impact LDT development. In this narrative review, we discuss the current status of fluid biomarkers used to diagnose early AD, their potential and limitations, and the impact caused by the FDA's decision and strategies to help developers navigate the complex changes in the regulatory landscape of LDTs.

Keywords: Alzheimer's disease; Amyloid beta; Clinical research; Dementia; FDA; Fluid biomarkers; LDT; NfL; Regulatory; Tau.

Publication types

  • Review

MeSH terms

  • Alzheimer Disease* / diagnosis
  • Alzheimer Disease* / metabolism
  • Amyloid beta-Peptides / metabolism
  • Biomarkers*
  • Early Diagnosis
  • Humans
  • United States
  • United States Food and Drug Administration*
  • tau Proteins / cerebrospinal fluid
  • tau Proteins / metabolism

Substances

  • Biomarkers
  • Amyloid beta-Peptides
  • tau Proteins