Lessons from a negative gene therapy trial for Duchenne muscular dystrophy
Nat Med
.
2025 Jan;31(1):37-38.
doi: 10.1038/s41591-024-03316-9.
Authors
Simone Spuler
1
,
Gian Domenico Borasio
2
,
Ulrike Grittner
3
Affiliations
1
Muscle Research Unit, Charité Universitätsmedizin Berlin and Max Delbrück Center, Berlin, Germany. simone.spuler@charite.de.
2
Palliative and Supportive Care Service, Lausanne University Hospital and University of Lausanne, Lausanne, Switzerland.
3
Institute of Biometry and Clinical Epidemiology, Charité Universitätsmedizin Berlin, Berlin, Germany.
PMID:
39385048
DOI:
10.1038/s41591-024-03316-9
No abstract available