Enzyme replacement with liposomes containing beta-galactosidase from Charonia lumpas in murine globoid cell leukodystrophy (twitcher)

Biochem Biophys Res Commun. 1985 Mar 15;127(2):663-7. doi: 10.1016/s0006-291x(85)80212-6.

Abstract

Enzyme replacement with liposomes containing beta-galactosidase obtained from charonia lumpas was carried out in murine globoid cell leukodystrophy (GLD). Charonia lumpas beta-galactosidase was able to hydrolyze galactocerebroside trapped into liposomes prepared from lecithin, cholesterol and sulfatide (molar ratio; 7:2:1). Liposomes containing charonia lumpas beta-galactosidase were successfully incorporated into the mouse tissues. 3H-galactocerebroside labeled liposomes were also incorporated into mouse liver, spleen and other tissues. The accumulation rate of 3H-galactocerebroside into twithcer mice liver and spleen was almost 40 to 100 times higher than those of controls and degraded to 70 to 80% of accumulated radioactivity of 3H-galactocerebroside by single injection of liposomes containing charonia lumpas beta-galactosidase. Results suggest that exogeneous enzyme trapped in liposomes can be useful for the correction of accumulated compound.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Aspergillus oryzae / enzymology
  • Brain / enzymology
  • Cattle
  • Cerebrosides / metabolism*
  • Disease Models, Animal
  • Fabaceae / enzymology
  • Galactosidases / administration & dosage*
  • Galactosylceramides / metabolism*
  • Hydrolysis
  • Kidney / enzymology
  • Leukodystrophy, Globoid Cell / drug therapy*
  • Leukodystrophy, Globoid Cell / enzymology
  • Liposomes / administration & dosage
  • Liver / enzymology
  • Mice
  • Mice, Neurologic Mutants
  • Mollusca / enzymology
  • Plants, Medicinal
  • Spleen / enzymology
  • beta-Galactosidase / administration & dosage*
  • beta-Galactosidase / therapeutic use

Substances

  • Cerebrosides
  • Galactosylceramides
  • Liposomes
  • galactocerebroside
  • Galactosidases
  • beta-Galactosidase