Application of fucosylation inhibitors for production of afucosylated antibody

Biotechnol Prog. 2024 May-Jun;40(3):e3438. doi: 10.1002/btpr.3438. Epub 2024 Feb 28.

Abstract

Fucosylation is an important quality attribute for therapeutic antibodies. Afucosylated antibodies exhibit higher therapeutic efficacies than their fucosylated counterparts through antibody-dependent cellular cytotoxicity (ADCC) mechanism. Since higher potency is beneficial in reducing dose or duration of the treatment, afucosylated antibodies have attracted a great deal of interest in biotherapeutics development. In this study, novel small molecules GDP-D-Rhamnose and its derivatives (Ac-GDP-D-Rhamnose and rhamnose sodium phosphate) were synthesized to inhibit the enzyme in the GDP-fucose synthesis pathway. Addition of these compounds into cell culture increased antibody afucosylation levels in a dose-dependent manner and had no significant impact on other protein quality attributes. A novel and effective mechanism to generate afucosylated antibody is demonstrated for biologics discovery, analytical method development, process development, and other applications.

Keywords: Chinese hamster ovary; afucosylation; antibody; cell culture media supplements; chemicals; glycosylation; inhibitors; small molecule.

MeSH terms

  • Animals
  • Antibodies, Monoclonal / biosynthesis
  • Antibodies, Monoclonal / chemistry
  • Antibody-Dependent Cell Cytotoxicity / drug effects
  • CHO Cells
  • Cricetulus*
  • Fucose* / chemistry
  • Fucose* / metabolism
  • Glycosylation
  • Guanosine Diphosphate Fucose / chemistry
  • Guanosine Diphosphate Fucose / metabolism
  • Humans
  • Rhamnose / chemistry
  • Rhamnose / metabolism

Substances

  • Fucose
  • Antibodies, Monoclonal
  • Rhamnose
  • Guanosine Diphosphate Fucose