Real-life data of Pasireotide LAR in acromegaly: a long-term follow-up

J Endocrinol Invest. 2024 Jul;47(7):1733-1741. doi: 10.1007/s40618-023-02275-1. Epub 2024 Jan 20.

Abstract

Objective: Pasireotide LAR (PAS-LAR) was released in Italy in 2017 to treat acromegaly patients resistant to SRLs (Somatostatin Receptors Ligands). The long-term follow-up data of PAS-LAR therapy in Italy are limited. This study aimed to evaluate the efficacy and safety of PAS-LAR in acromegaly.

Design: Patients with acromegaly in PAS-LAR treatment were enrolled in three tertiary Italian endocrinological centers and evaluated by a retrospective observational real-life multicentre study.

Methods: Patients have been studied before (baseline) and 1, 6, 12, 24 and > 36 months after PAS-LAR start. Clinical, biochemical, and pituitary magnetic resonance data were collected, along with information on adverse events. Acromegaly disease activity was classified according to the IGF-1 index (normal value < 1.0).

Results: Fifty patients (female 23) were enrolled. PAS-LAR treatment (mean follow-up 24 ± 16 months) significantly decreased IGF-1 levels (IGF-1 index baseline vs last visit: 1.9 ± 0.6 vs 1.2 ± 0.6, p < 0.0001). At the last visit, 67% of patients had controlled disease, and 44% showed a decrease in tumor volume. Clinical and biochemical efficacy was observed as early as after 1-month of PAS-LAR treatment (IGF-1 index baseline vs 1-month: 1.9 ± 0.6 vs 1.4 ± 0.7, p < 0.0001). Also, 50% of patients referred headache improvement or disappearance. Fifteen patients discontinued PAS-LAR due to failure of treatment and poor glycaemic control. The prevalence of diabetes increased from 33% at the baseline to 54% at the last visit (p = 0.0072).

Conclusion: In real-life settings, PAS-LAR significantly decreases symptoms, IGF-1 levels, and the size of adenoma in patients with acromegaly resistant to SRLs. Beneficial effects may occur early after the first injection.

Keywords: GH; Headache; IGF-1; PAS-LAR.

Publication types

  • Observational Study
  • Multicenter Study

MeSH terms

  • Acromegaly* / drug therapy
  • Adult
  • Aged
  • Female
  • Follow-Up Studies
  • Growth Hormone-Secreting Pituitary Adenoma / complications
  • Growth Hormone-Secreting Pituitary Adenoma / drug therapy
  • Human Growth Hormone / blood
  • Humans
  • Insulin-Like Growth Factor I / analysis
  • Insulin-Like Growth Factor I / metabolism
  • Italy / epidemiology
  • Male
  • Middle Aged
  • Retrospective Studies
  • Somatostatin* / administration & dosage
  • Somatostatin* / analogs & derivatives
  • Somatostatin* / therapeutic use
  • Treatment Outcome

Substances

  • pasireotide
  • Somatostatin
  • Insulin-Like Growth Factor I
  • Human Growth Hormone