Mission possible: Gene therapy for inherited metabolic diseases

Affiliations

• ¹ Great Ormond Street Institute of Child Health, University College London, London, UK.
• ² Great Ormond Street Hospital for Children NHS Trust, London, UK.
• ³ National Institute of Health Research Great Ormond Street Biomedical Research Centre, London, UK.
• ⁴ Metabolic Medicine Branch, National Human Genome Research Institute, National Institutes of Health (NIH), Bethesda, Maryland, USA.