1 Department of Pediatrics, University of Utah School of Medicine, Salt Lake City, Utah; Center for Personalized Medicine, Primary Children's Hospital, Salt Lake City, Utah. Electronic address: joshua.bonkowsky@hsc.utah.edu.
2 Intermountain Health, Salt Lake City, Utah.
3 Department of Pediatrics, University of Utah School of Medicine, Salt Lake City, Utah.
4 Leukodystrophy Care Network, Buffalo, New York.
5 Division of Transplant and Cellular Therapy, Department of Pediatrics, Duke University School of Medicine, Durham, North Carolina.
6 New York State Department of Health, Wadsworth Center, Albany, New York.