Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy

N Engl J Med. 2023 Dec 7;389(23):2211. doi: 10.1056/NEJMc2312288.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Humans
  • Muscular Dystrophy, Duchenne* / genetics
  • Muscular Dystrophy, Duchenne* / therapy
  • Patients