Developments in stem cell-derived islet replacement therapy for treating type 1 diabetes

Cell Stem Cell. 2023 May 4;30(5):530-548. doi: 10.1016/j.stem.2023.04.002.

Abstract

The generation of islet-like endocrine clusters from human pluripotent stem cells (hPSCs) has the potential to provide an unlimited source of insulin-producing β cells for the treatment of diabetes. In order for this cell therapy to become widely adopted, highly functional and well-characterized stem cell-derived islets (SC-islets) need to be manufactured at scale. Furthermore, successful SC-islet replacement strategies should prevent significant cell loss immediately following transplantation and avoid long-term immune rejection. This review highlights the most recent advances in the generation and characterization of highly functional SC-islets as well as strategies to ensure graft viability and safety after transplantation.

Keywords: CRISPR; SC-islets; bioreactors; clinical trials; critical quality attributes; cryopreservation; diabetes; differentiation; distribution; encapsulation; immune tolerance; insulin; pancreas; safety; scale-up; single-cell sequencing; stem cells; stress; therapy; transplantation.

Publication types

  • Review
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cell Differentiation
  • Diabetes Mellitus, Type 1* / therapy
  • Humans
  • Insulin-Secreting Cells*
  • Islets of Langerhans*
  • Pluripotent Stem Cells*