A Novel Monoclonal Antibody Degrades the Thyrotropin Receptor Autoantibodies in Graves' Disease

Endocr Pract. 2023 Jul;29(7):553-559. doi: 10.1016/j.eprac.2023.04.002. Epub 2023 Apr 18.

Abstract

Objective: Autoantibodies against the thyrotropin receptor (TSH-R-Ab) are key mediators for the pathogenesis of Graves' disease (GD). TSH-R-Ab degradation was evaluated using several immunoassays within an exploratory, controlled trial in patients with GD receiving a monoclonal antibody (mAb) targeting the neonatal crystallizable fragment receptor (FcRn).

Methods: Serial measurements of TSH-R-Ab serum levels were performed using 3 different binding and cell-based assays in patients with GD either on medication or on placebo.

Results: In contrast to the placebo group, in which no changes were observed, a 12-week mAb therapy led to an early and significant decrease (>60%) in the serum TSH-R-Ab levels in patients with thyroidal and extrathyroidal GD, as unanimously shown in all 3 assays. These marked changes were noted already at week 7 post baseline (P <.0001 for the binding immunoassay and for the luciferase (readout) bioassay). The 3 TSH-R-Ab binding and bioassays were highly correlated in the samples of both study groups (binding immunoassay vs luciferase bioassay, r =.91, P <.001, binding vs cyclic adenosine monophosphate (cAMP) bioassay, r = 0.86, P <.001, and luciferase vs cAMP bioassay, r = 0.71, P =.006). The serological results correlated with the course of the extrathyroidal clinical parameters of GD, that is, clinical activity score and proptosis.

Conclusion: Targeting the FcRn markedly reduces the disease-specific TSH-R-Ab in patients with GD. The novel and rapid TSH-R-Ab bioassay improves diagnosis and management of patients with GD.

Keywords: autoantibody degradation; autoimmune thyroid disease; thyrotropin receptor autoantibodies.

Publication types

  • Controlled Clinical Trial

MeSH terms

  • Antibodies, Monoclonal / therapeutic use
  • Autoantibodies
  • Graves Disease* / diagnosis
  • Graves Disease* / drug therapy
  • Humans
  • Immunoglobulins, Thyroid-Stimulating
  • Infant, Newborn
  • Long-Acting Thyroid Stimulator* / therapeutic use
  • Receptors, Thyrotropin
  • Thyrotropin

Substances

  • Antibodies, Monoclonal
  • Autoantibodies
  • Immunoglobulins, Thyroid-Stimulating
  • Long-Acting Thyroid Stimulator
  • Receptors, Thyrotropin
  • Thyrotropin