The ubiquitin-dependent ATPase p97 removes cytotoxic trapped PARP1 from chromatin

Nat Cell Biol. 2022 Jan;24(1):62-73. doi: 10.1038/s41556-021-00807-6. Epub 2022 Jan 10.

Abstract

Poly (ADP-ribose) polymerase (PARP) inhibitors elicit antitumour activity in homologous recombination-defective cancers by trapping PARP1 in a chromatin-bound state. How cells process trapped PARP1 remains unclear. Using wild-type and a trapping-deficient PARP1 mutant combined with rapid immunoprecipitation mass spectrometry of endogenous proteins and Apex2 proximity labelling, we delineated mass spectrometry-based interactomes of trapped and non-trapped PARP1. These analyses identified an interaction between trapped PARP1 and the ubiquitin-regulated p97 ATPase/segregase. We found that following trapping, PARP1 is SUMOylated by PIAS4 and subsequently ubiquitylated by the SUMO-targeted E3 ubiquitin ligase RNF4, events that promote recruitment of p97 and removal of trapped PARP1 from chromatin. Small-molecule p97-complex inhibitors, including a metabolite of the clinically used drug disulfiram (CuET), prolonged PARP1 trapping and enhanced PARP inhibitor-induced cytotoxicity in homologous recombination-defective tumour cells and patient-derived tumour organoids. Together, these results suggest that p97 ATPase plays a key role in the processing of trapped PARP1 and the response of tumour cells to PARP inhibitors.

Publication types

  • Research Support, N.I.H., Intramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Cell Line, Tumor
  • Chromatin / metabolism*
  • Disulfiram / analogs & derivatives
  • Disulfiram / pharmacology
  • HCT116 Cells
  • HeLa Cells
  • Humans
  • MCF-7 Cells
  • Neoplasms / drug therapy
  • Nuclear Proteins / metabolism
  • Poly (ADP-Ribose) Polymerase-1 / antagonists & inhibitors*
  • Poly (ADP-Ribose) Polymerase-1 / metabolism*
  • Poly(ADP-ribose) Polymerase Inhibitors / pharmacology*
  • Poly-ADP-Ribose Binding Proteins / metabolism
  • Protein Inhibitors of Activated STAT / metabolism
  • Sumoylation
  • Transcription Factors / metabolism
  • Ubiquitination
  • Valosin Containing Protein / metabolism*

Substances

  • Chromatin
  • Nuclear Proteins
  • PIAS4 protein, human
  • Poly(ADP-ribose) Polymerase Inhibitors
  • Poly-ADP-Ribose Binding Proteins
  • Protein Inhibitors of Activated STAT
  • RNF4 protein, human
  • Transcription Factors
  • PARP1 protein, human
  • Poly (ADP-Ribose) Polymerase-1
  • VCP protein, human
  • Valosin Containing Protein
  • Disulfiram