Validation of a next-generation sequencing assay for the detection of EGFR mutations in cell-free circulating tumor DNA

Exp Mol Pathol. 2021 Dec:123:104685. doi: 10.1016/j.yexmp.2021.104685. Epub 2021 Sep 21.

Abstract

Detection of EGFR mutations from blood plasma represents a gentle, non-invasive alternative to rebiopsy and can therefore be used for therapy monitoring of non-small-cell lung cancer (NSCLC) patients. The aim of this project was to investigate whether the Reveal ctDNA™ 28 NGS assay (ArcherDX, Boulder, CO), has a comparable sensitivity and specificity to droplet digital PCR (ddPCR, gold-standard) and is therefore suitable for therapy monitoring of progressing lung cancer patients. First, we validated the NGS assay with a commercially available reference material (SeraCare, Massachusetts, US). Using an input of 22 ng, a sensitivity of 96% and a specificity of 100% could be achieved for variant allele frequencies (VAF) of 0.5%. For variants at a VAF of 0.1% the sensitivity was substantially reduced. Next, 28 plasma samples from 16 patients were analyzed and results were compared to existing ddPCR data. This comparative analysis of patient samples revealed a concordance of 91% between NGS and ddPCR. These results confirm that the Reveal ctDNA™ 28 NGS assay can be used for therapy monitoring of patients under TKI therapy. However, due to the slightly superior sensitivity of ddPCR, a combination of NGS (with broad coverage of a large number of genomic loci) and ddPCR (with targeted highly sensitive detection of specific mutations) might be the ideal approach.

Keywords: Blood; Cell free DNA; Digital droplet PCR; EGFR; Liquid biopsy; Lung cancer; Mutation; NGS; NSCLC; Next generation sequencing; T790M; cfDNA; ctDNA; ddPCR.

MeSH terms

  • Adult
  • Aged
  • Biomarkers, Tumor / blood
  • Carcinoma, Non-Small-Cell Lung / blood*
  • Carcinoma, Non-Small-Cell Lung / genetics
  • Carcinoma, Non-Small-Cell Lung / pathology
  • Cell-Free Nucleic Acids / blood*
  • Cell-Free Nucleic Acids / genetics
  • Circulating Tumor DNA / blood*
  • Circulating Tumor DNA / genetics
  • ErbB Receptors / blood
  • ErbB Receptors / genetics
  • Female
  • High-Throughput Nucleotide Sequencing
  • Humans
  • Liquid Biopsy
  • Male
  • Middle Aged
  • Mutation / genetics

Substances

  • Biomarkers, Tumor
  • Cell-Free Nucleic Acids
  • Circulating Tumor DNA
  • EGFR protein, human
  • ErbB Receptors