The MED13L haploinsufficiency syndrome associated with de novo nonsense variant (P.GLN1981*)

J Mother Child. 2021 Apr 30;24(3):32-36. doi: 10.34763/jmotherandchild.20202403.2021.d-20-00003.

Abstract

The Mediator complex subunit 13-like is a part of the large Mediator complex. Recently, a large number of patients were diagnosed with mutations in this gene, which makes it one of the most frequent causes of syndromic intellectual disability. In this work, we report a patient with a novel de novo likely pathogenic variant c.5941C>T, p.(Gln1981*) in the MED13L gene with severe intellectual disability and facial dysmorphism. Uncommon findings like lack of speech, strabismus and self-destructive behaviour present in our patient allowed us to further define the phenotypic spectrum of mental retardation and distinctive facial features with or without cardiac defects syndrome.

Keywords: MED13L; haploinsufficiency; intellectual disability; loss-of-function mutation.

Publication types

  • Case Reports

MeSH terms

  • Abnormalities, Multiple / diagnosis*
  • Abnormalities, Multiple / genetics*
  • Abnormalities, Multiple / physiopathology*
  • Child
  • Genetic Variation
  • Haploinsufficiency*
  • Humans
  • Intellectual Disability / diagnosis
  • Intellectual Disability / genetics*
  • Intellectual Disability / physiopathology
  • Loss of Function Mutation*
  • Male
  • Mediator Complex / genetics*
  • Mutation
  • Phenotype

Substances

  • Mediator Complex

Grants and funding

This study was supported by the National Science Centre, Poland 2012/07/B/NZ4/01764 and 2015/19/B/NZ2/01824