Targeting RNA-binding proteins in acute and chronic leukemia

Leukemia. 2021 Feb;35(2):360-376. doi: 10.1038/s41375-020-01066-4. Epub 2020 Nov 4.

Abstract

RNA-binding proteins (RBPs) play a crucial role in cellular physiology by regulating RNA processing, translation, and turnover. In neoplasms, RBP support of cancer-relevant expression of alternatively spliced, modified, and stabilized mRNA transcripts is essential to self-renewal, proliferation, and adaptation to stress. In this review, we assess the impact of key families of RBPs in leukemogenesis, review progress in targeting those proteins with small molecules, and discuss how multilevel composition of posttranscriptional regulation of gene expression could be used for potential therapies in acute and chronic leukemia.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Acute Disease
  • Animals
  • Antineoplastic Agents / pharmacology*
  • Chronic Disease
  • Gene Expression Regulation, Leukemic*
  • Humans
  • Leukemia / drug therapy
  • Leukemia / metabolism
  • Leukemia / pathology*
  • Molecular Targeted Therapy*
  • RNA Processing, Post-Transcriptional*
  • RNA-Binding Proteins / antagonists & inhibitors*

Substances

  • Antineoplastic Agents
  • RNA-Binding Proteins