Re: "Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy" by Wilson and Flotte

Hum Gene Ther. 2020 Aug;31(15-16):787. doi: 10.1089/hum.2020.217.
No abstract available

Publication types

  • Letter
  • Comment

MeSH terms

  • Genetic Therapy
  • Humans
  • Myopathies, Structural, Congenital* / genetics
  • Myopathies, Structural, Congenital* / therapy