Reply to Chacko
et al.
: Limited Assessment of Respiratory Muscle Response to Nusinersen Treatment in Infants with Spinal Muscular Atrophy
Am J Respir Crit Care Med
.
2020 Mar 1;201(5):624-626.
doi: 10.1164/rccm.201910-2022LE.
Authors
Antonella LoMauro
1
,
Chiara Mastella
2
,
Katia Alberti
2
,
Riccardo Masson
3
,
Andrea Aliverti
1
,
Giovanni Baranello
3
4
Affiliations
1
Politecnico di MilanoMilan, Italy.
2
Fondazione IRCCS Cà' Granda Ospedale Maggiore PoliclinicoMilan, Italy.
3
Fondazione IRCCS Istituto Neurologico Carlo BestaMilan, Italyand.
4
UCL Great Ormond Street Institute of Child Health LondonLondon, United Kingdom.
PMID:
31747301
PMCID:
PMC7047463
DOI:
10.1164/rccm.201910-2022LE
No abstract available
Publication types
Letter
Comment
MeSH terms
Humans
Infant
Muscular Atrophy, Spinal*
Oligonucleotides
Respiratory Muscles
Spinal Muscular Atrophies of Childhood*
Substances
Oligonucleotides
nusinersen