Lethal osteogenesis imperfecta resulting from a single nucleotide change in one human pro alpha 1(I) collagen allele

Proc Natl Acad Sci U S A. 1986 Aug;83(16):6045-7. doi: 10.1073/pnas.83.16.6045.

Abstract

We have characterized a mutation in a pro alpha 1(I) procollagen gene (COL1A1) that results in lethal (type II) osteogenesis imperfecta. The mutation is a single base change that results in a cysteine-for-glycine substitution at position 988 of the triple-helical portion of half of the alpha 1(I) chains of type I collagen. The mutation thus disrupts the (Gly-Xaa-Yaa)n pattern necessary for triple-helix formation, where Xaa and Yaa are other amino acids. These experiments establish the minimal mutation in a type I collagen gene capable of producing lethal disease, and the lethality demonstrates a selective mechanism for the stringent maintenance of the collagen gene structure.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Alleles*
  • Amino Acid Sequence
  • Base Sequence
  • Cloning, Molecular
  • DNA Restriction Enzymes
  • Genes*
  • Genes, Lethal*
  • Humans
  • Infant
  • Mutation
  • Osteogenesis Imperfecta / genetics*
  • Procollagen / genetics*

Substances

  • Procollagen
  • DNA Restriction Enzymes