Gene Therapy as a Curative Option for β-Thalassemia

N Engl J Med. 2018 Apr 19;378(16):1551-1552. doi: 10.1056/NEJMe1802169.
No abstract available

Publication types

  • Editorial
  • Comment

MeSH terms

  • Genetic Therapy
  • Genetic Vectors
  • Humans
  • Lentivirus / genetics*
  • beta-Thalassemia*