Germline deletion of CIN85 in humans with X chromosome-linked antibody deficiency

J Exp Med. 2018 May 7;215(5):1327-1336. doi: 10.1084/jem.20170534. Epub 2018 Apr 10.

Abstract

Ubiquitously expressed Cbl-interacting protein of 85 kD (CIN85) is a multifunctional adapter molecule supposed to regulate numerous cellular processes that are critical for housekeeping as well as cell type-specific functions. However, limited information exists about the in vivo roles of CIN85, because only conditional mouse mutants with cell type-specific ablation of distinct CIN85 isoforms in brain and B lymphocytes have been generated so far. No information is available about the roles of CIN85 in humans. Here, we report on primary antibody deficiency in patients harboring a germline deletion within the CIN85 gene on the X chromosome. In the absence of CIN85, all immune cell compartments developed normally, but B lymphocytes showed intrinsic defects in distinct effector pathways of the B cell antigen receptor, most notably NF-κB activation and up-regulation of CD86 expression on the cell surface. These results reveal nonredundant functions of CIN85 for humoral immune responses.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adaptor Proteins, Signal Transducing / deficiency
  • Adaptor Proteins, Signal Transducing / genetics*
  • Antibodies / metabolism*
  • B-Lymphocytes / immunology
  • Calcium / metabolism
  • Chromosomes, Human, X / genetics*
  • Gene Deletion*
  • Germ Cells / metabolism*
  • Humans
  • Immunoglobulin G / blood
  • Immunologic Deficiency Syndromes / blood
  • Immunologic Deficiency Syndromes / genetics*
  • Immunophenotyping
  • Lymphocyte Activation / immunology
  • Male
  • NF-kappa B / metabolism
  • Receptors, Antigen, T-Cell / metabolism
  • Siblings
  • Signal Transduction

Substances

  • Adaptor Proteins, Signal Transducing
  • Antibodies
  • Immunoglobulin G
  • NF-kappa B
  • Receptors, Antigen, T-Cell
  • SH3KBP1 protein, human
  • Calcium