Antitumor activity of CD56-chimeric antigen receptor T cells in neuroblastoma and SCLC models

Oncogene. 2018 Jul;37(27):3686-3697. doi: 10.1038/s41388-018-0187-2. Epub 2018 Apr 6.

Abstract

The CD56 antigen (NCAM-1) is highly expressed on several malignancies with neuronal or neuroendocrine differentiation, including small-cell lung cancer and neuroblastoma, tumor types for which new therapeutic options are needed. We hypothesized that CD56-specific chimeric antigen receptor (CAR) T cells could target and eliminate CD56-positive malignancies. Sleeping Beauty transposon-generated CD56R-CAR T cells exhibited αβT-cell receptors, released antitumor cytokines upon co-culture with CD56+ tumor targets, demonstrated a lack of fratricide, and expression of cytolytic function in the presence of CD56+ stimulation. The CD56R-CAR+ T cells are capable of killing CD56+ neuroblastoma, glioma, and SCLC tumor cells in in vitro co-cultures and when tested against CD56+ human xenograft neuroblastoma models and SCLC models, CD56R-CAR+ T cells were able to inhibit tumor growth in vivo. These results indicate that CD56-CARs merit further investigation as a potential treatment for CD56+ malignancies.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • CD56 Antigen / genetics
  • CD56 Antigen / metabolism*
  • Cell Line, Tumor
  • Glioma / pathology
  • Glioma / therapy*
  • Humans
  • Lung Neoplasms / pathology
  • Lung Neoplasms / therapy*
  • Lymphocyte Activation / immunology
  • Mice
  • Mice, Inbred NOD
  • Mice, Nude
  • Neuroblastoma / pathology
  • Neuroblastoma / therapy*
  • Receptors, Chimeric Antigen / metabolism*
  • Small Cell Lung Carcinoma / pathology
  • Small Cell Lung Carcinoma / therapy*
  • T-Lymphocytes / immunology*
  • T-Lymphocytes / transplantation*
  • Transposases / metabolism
  • Xenograft Model Antitumor Assays

Substances

  • CD56 Antigen
  • NCAM1 protein, human
  • Receptors, Chimeric Antigen
  • Transposases
  • sleeping beauty transposase, human