First-in-human study to assess the safety, pharmacokinetics and pharmacodynamics of BMS-962212, a direct, reversible, small molecule factor XIa inhibitor in non-Japanese and Japanese healthy subjects

Br J Clin Pharmacol. 2018 May;84(5):876-887. doi: 10.1111/bcp.13520. Epub 2018 Mar 5.

Abstract

Aims: The aims of the present study were to assess the safety, pharmacokinetics (PK) and pharmacodynamics (PD) of BMS-962212, a first-in-class factor XIa inhibitor, in Japanese and non-Japanese healthy subjects.

Methods: This was a randomized, placebo-controlled, double-blind, sequential, ascending-dose study of 2-h (part A) and 5-day (part B) intravenous (IV) infusions of BMS-962212. Part A used four doses (1.5, 4, 10 and 25 mg h-1 ) of BMS-962212 or placebo in a 6:2 ratio per dose. Part B used four doses (1, 3, 9 and 20 mg h-1 ) enrolling Japanese (n = 4 active, n = 1 placebo) and non-Japanese (n = 4 active, n = 1 placebo) subjects per dose. The PK, PD, safety and tolerability were assessed throughout the study.

Results: BMS-962212 was well tolerated; there were no signs of bleeding, and adverse events were mild. In parts A and B, BMS-962212 demonstrated dose proportionality. The mean half-life in parts A and B ranged from 2.04 to 4.94 h and 6.22 to 8.65 h, respectively. Exposure-dependent changes were observed in the PD parameters, activated partial thromboplastin time (aPTT) and factor XI clotting activity (FXI:C). The maximum mean aPTT and FXI:C change from baseline at 20 mg h-1 in part B was 92% and 90%, respectively. No difference was observed in weight-corrected steady-state concentrations, aPTT or FXI:C between Japanese and non-Japanese subjects (P > 0.05).

Conclusion: BMS-962212 has tolerability, PK and PD properties suitable for investigational use as an acute antithrombotic agent in Japanese or non-Japanese subjects.

Keywords: Japanese; anticoagulation; factor XIa inhibition; pharmacodynamics; pharmacokinetics.

Publication types

  • Clinical Trial, Phase I
  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Asian People / statistics & numerical data
  • Dose-Response Relationship, Drug
  • Double-Blind Method
  • Female
  • Fibrinolytic Agents / pharmacology
  • Healthy Volunteers
  • Humans
  • Infusions, Intravenous
  • Isoquinolines / administration & dosage
  • Isoquinolines / adverse effects*
  • Isoquinolines / pharmacokinetics*
  • Isoquinolines / pharmacology*
  • Male
  • Middle Aged
  • Partial Thromboplastin Time / statistics & numerical data
  • White People / statistics & numerical data
  • Young Adult
  • para-Aminobenzoates / administration & dosage
  • para-Aminobenzoates / adverse effects*
  • para-Aminobenzoates / pharmacokinetics*
  • para-Aminobenzoates / pharmacology*

Substances

  • BMS-962212
  • Fibrinolytic Agents
  • Isoquinolines
  • para-Aminobenzoates