Clinic-Based Validation of Cerebrospinal Fluid Biomarkers with Florbetapir PET for Diagnosis of Dementia

J Alzheimers Dis. 2018;61(1):135-143. doi: 10.3233/JAD-170753.

Abstract

Background: Cerebrospinal fluid (CSF) biomarker studies have shown variable accuracy for diagnosis of Alzheimer's disease (AD); therefore, internal validation is recommended.

Objective: To investigate the correlation between CSF biomarkers and cerebral 18-Florbetapir positron emission tomography (Amyloid-PET) and calculate their sensitivity and specificity to obtain the optimal clinical cut-off points to diagnose the etiology of cognitive impairment.

Methods: We performed Amyloid-PET scans and CSF biomarker levels analyses in 68 subjects (50 with mild cognitive impairment, 11 with AD dementia, and 7 with non-AD dementia). Visual examination of Amyloid-PET scans was performed. CSF analyses were performed using standard sandwich ELISA.

Results: Amyloid-PET was positive in 36 subjects, negative in 26, and inconclusive in 6. Optimal clinical cut-off points for CSF markers were the following: amyloid-β 1-42 (Aβ42) = 629 pg/ml, total tau (t-tau) = 532 pg/ml, phosphorylated tau (p-tau) = 88 pg/ml, and t-tau/Aβ42 ratio = 0.58. T-tau/Aβ42 ratio showed the best sensitivity and specificity (92 and 84%, respectively). T-tau and p-tau CSF levels (r2 = 0.867) followed by the t-tau and t-tau/Aβ42 CSF ratio (r2 = 0.666) showed the strongest inter-marker correlation. Interestingly, subjects with inconclusive Amyloid-PET showed intermediate values for all CSF markers between negative and positive Amyloid-PET groups.

Conclusions: CSF t-tau/Aβ42 ratio appears to be the most accurate AD CSF marker. The presence of intermediate values for CSF markers among the subjects with inconclusive Amyloid-PET suggests the presence of other dementias associated with AD pathology or intermediate phenotypes.

Keywords: Alzheimer’s disease; amyloid; apolipoprotein E; cerebrospinal fluid; positron emission tomography.

MeSH terms

  • Aged
  • Amyloid beta-Peptides / cerebrospinal fluid
  • Analysis of Variance
  • Aniline Compounds / metabolism*
  • Apolipoproteins E / genetics
  • Biomarkers / cerebrospinal fluid*
  • Cognition Disorders / etiology
  • Dementia / cerebrospinal fluid*
  • Dementia / complications
  • Dementia / diagnostic imaging*
  • Dementia / genetics
  • Ethylene Glycols / metabolism*
  • Female
  • Humans
  • Male
  • Middle Aged
  • Peptide Fragments / cerebrospinal fluid
  • Positron-Emission Tomography
  • tau Proteins / cerebrospinal fluid

Substances

  • Amyloid beta-Peptides
  • Aniline Compounds
  • Apolipoproteins E
  • Biomarkers
  • Ethylene Glycols
  • Peptide Fragments
  • amyloid beta-protein (1-42)
  • tau Proteins
  • florbetapir